“This is nothing short of a miracle," mom Shante Stagg told TODAY of a gene therapy that has helped her son who has a rare health condition. After a complicated birth, Jamell Stagg Jr.’s parents ...
Texas Children's is pleased to announce that a three-year-old girl has been successfully treated with the first-ever FDA-approved gene therapy treatment for AADC deficiency. Aromatic l-amino acid ...
CAMBRIDGE, Mass., Nov. 07, 2018 (GLOBE NEWSWIRE) -- Voyager Therapeutics, Inc. (NASDAQ: VYGR), a clinical-stage gene therapy company focused on developing life-changing treatments for severe ...
SOUTH PLAINFIELD, N.J., Oct. 22, 2020 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) and the AADC Family Network today announced that Oct. 23, 2020, has been officially designated as the first ...
(RTTNews) - PTC Therapeutics Inc. (PTCT), on Thursday, announced that it has completed the Scientific Advisory Group and Oral Explanation meetings for its gene therapy treatment for AADC deficiency or ...
SAN DIEGO and CAMBRIDGE, Mass., March 28, 2019 (GLOBE NEWSWIRE) -- Neurocrine Biosciences, Inc. (NASDAQ:NBIX) and Voyager Therapeutics, Inc. (NASDAQ:VYGR) today announced the publication of interim ...
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